Gene Therapy for Muscular Dystrophy Advances

Scientists say they could be on the cusp of having a treatment for muscular dystrophy, an inherited disease that gradually weakens and destroys muscles and currently has no cure. The researchers focused on the most common form of the disease, which is caused by a genetic mutation that disrupts the production of a protein that strengthens and protects muscle fibers. Muscle weakness typically begins before a child turns 5, and boys are most likely to be affected. Because the damaged gene...

© La Voix de l'Amérique - jeudi 22 octobre 2015