Observatoire des droits humains (anglais seulement)

New hope for Huntington’s families as gene therapy shows remarkable results

(Version anglaise seulement)

par Åsa Petersén, Professor of Neuroscience, Lund University

A company called uniQure has announced promising results from a trial of a new gene therapy for Huntington’s disease. The news has spread quickly through families affected by this condition, who have been desperately waiting for a treatment that can stop or slow down this devastating illness.

Huntington’s disease is a fatal brain disorder that runs in families, caused by a faulty gene that produces a protein called huntingtin. The disease typically begins to cause symptoms in people between 30…

Lire l'article complet