New gene therapies may soon treat dozens of rare diseases, but million-dollar price tags will put them out of reach for many

Zolgensma – which treats spinal muscular atrophy, a rare genetic disease that damages nerve cells, leading to muscle decay – is currently the most expensive drug in the world. A one-time treatment of the life-saving drug for a young child costs…

© La Conversation - mardi 31 août 2021